Preclinical studies for plant-based oral enzyme replacement therapy (Oral-ERT) in Pompe disease knockout mice with transgenic tobacco seeds expressing human GAA (tobrhGAA)

Added 67 days ago (12.11.2021)
Authors: Martiniuk, F., Martiniuk, J., Mack, A., Voronin, G., Miller, S., Reimer, D., Rossi, N., Bird, L., Gupta, R., Nigro, M., Saleh, S., Meinke, P., Schoser, B., Wu, F., Tchou-Wong, K. M., Kambitsis, A., Arvanitopoulos, J., Arvanitopoulos, E.
Source: bioRxiv
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