Central and peripheral delivery of AAV9-SMN target different pathomechanisms in a mouse model of spinal muscular atrophy

Added 192 days ago (09.11.2021)

Authors: Reilly, A. N., Deguise, M., Beauvais, A., Yaworski, R., Thebault, S., Tessier, D. R., Tabard-Cossa, V., Hensel, N., Schneider, B. L., Kothary, R.